# Holder Name Position Position Change $ Market Value % Port % O/S Rpt Date
1 UBS Securities LLC 4,183,385 4,020,831 462,849,716.4 0.1888 5.3751 09/30/2025
2 Darwin Global Management Ltd. 3,164,501 3,164,501 350,120,390.64 6.2521 4.066 09/30/2025
3 Point72 Asset Management LP 2,925,352 2,895,934 323,660,945.28 0.589 3.7587 09/30/2025
4 Cormorant Asset Management LP 1,950,000 -180,000 215,748,000 11.7123 2.5055 09/30/2025
5 Paradigm BioCapital Advisors LP 1,564,196 1,564,196 173,062,645.44 3.99 2.0098 09/30/2025
6 Caligan Partners LP 1,451,924 182,805 160,640,871.36 17.4008 1.8655 09/30/2025
7 Fidelity Management & Research Co. LLC 1,430,673 1,430,673 158,289,660.72 0.0088 1.8382 09/30/2025
8 Adar1 Capital Management LLC 1,350,826 -859,193 149,455,388.64 13.9601 1.7356 09/30/2025
9 Octagon Capital Advisors LP 1,325,000 95,000 146,598,000 16.6703 1.7025 09/30/2025
10 Millennium Management LLC 1,100,030 112,616 121,707,319.2 0.0948 1.4134 09/30/2025
11 Vestal Point Capital LP 1,000,000 1,000,000 110,640,000 3.98 1.2849 09/30/2025
12 Adage Capital Management LP 977,629 977,629 108,164,872.56 0.1641 1.2561 09/30/2025
13 Baker Bros. Advisors LP 875,796 875,796 96,898,069.44 0.4856 1.1253 09/30/2025
14 Farallon Capital Management LLC 805,000 805,000 89,065,200 0.4447 1.0343 09/30/2025
15 Saturn V Capital Management LP 801,224 248,298 88,647,423.36 14.446 1.0295 09/30/2025
# Holder Name Position Position Change $ Market Value % Port % O/S Rpt Date
1 Xtrackers SICAV - MSCI World Swap UCITS ETF 764,899 764,899 84,628,425.36 0.7933 0.9828 11/28/2025
2 abrdn World Healthcare Fund 397,578 -312,938 43,988,029.92 7.4097 0.5108 10/31/2025
3 Eventide Healthcare & Life Sciences Fund 396,904 396,904 43,913,458.56 2.5915 0.51 09/30/2025
4 Fidelity Growth Company Commingled Pool 374,807 374,807 41,468,646.48 0.0386 0.4816 10/31/2025
5 Alger Institutional Funds - Focus Equity Fund 314,786 314,786 34,827,923.04 0.788 0.4045 10/31/2025
6 FTIF SICAV - Biotechnology Discovery Fund 307,602 -565,693 34,033,085.28 1.9249 0.3952 10/31/2025
7 Fidelity Growth Company Fund 298,473 298,473 33,023,052.72 0.0414 0.3835 10/31/2025
8 Alger Funds II - Alger Spectra Fund 258,451 258,451 28,595,018.64 0.6466 0.3321 10/31/2025
9 FCP Medical - BioHealth 201,222 201,222 22,263,202.08 2.3202 0.2585 09/30/2025
10 Franklin Biotechnology Discovery Fund 173,710 -323,982 19,219,274.4 1.8597 0.2232 10/31/2025
11 Alger Institutional Funds - Capital Appreciation Inst. Fund 173,148 173,148 19,157,094.72 0.5907 0.2225 10/31/2025
12 Alger Small Cap Focus Fund 154,768 154,768 17,123,531.52 1.846 0.1989 10/31/2025
13 Westfield Small/Mid Cap Growth Equity 138,500 138,500 15,323,640 0.9338 0.178 10/31/2025
14 Lord Abbett Developing Growth Fund 138,439 138,439 15,316,890.96 0.6833 0.1779 07/31/2025
15 Alger Capital Appreciation Fund 128,898 128,898 14,261,274.72 0.5449 0.1656 10/31/2025
# Holder Name Position Position Change $ Market Value % Port % O/S Rpt Date
1 UBS Securities LLC 4,183,385 4,020,831 462,849,716.4 0.1888 5.3751 09/30/2025
2 Darwin Global Management Ltd. 3,164,501 3,164,501 350,120,390.64 6.2521 4.066 09/30/2025
3 Point72 Asset Management LP 2,925,352 2,895,934 323,660,945.28 0.589 3.7587 09/30/2025
4 Paradigm BioCapital Advisors LP 1,564,196 1,564,196 173,062,645.44 3.99 2.0098 09/30/2025
5 Fidelity Management & Research Co. LLC 1,430,673 1,430,673 158,289,660.72 0.0088 1.8382 09/30/2025
6 Vestal Point Capital LP 1,000,000 1,000,000 110,640,000 3.98 1.2849 09/30/2025
7 Adage Capital Management LP 977,629 977,629 108,164,872.56 0.1641 1.2561 09/30/2025
8 Baker Bros. Advisors LP 875,796 875,796 96,898,069.44 0.4856 1.1253 09/30/2025
9 Farallon Capital Management LLC 805,000 805,000 89,065,200 0.4447 1.0343 09/30/2025
10 Nationale-Nederlanden PTE SA 731,523 731,523 80,935,704.72 0.5017 0.9399 09/30/2025
# Holder Name Position Position Change $ Market Value % Port % O/S Rpt Date
1 Deep Track Capital LP 0 -3,579,209 0 0 0
2 Great Point Partners LLC 150,000 -1,488,111 16,596,000 5.4203 0.1927 09/30/2025
3 VHCP Management LLC 0 -998,570 0 0 0
4 Allostery Investments LP 167,350 -932,304 18,515,604 64.7881 0.215 06/30/2025
5 Nantahala Capital Management LLC 557,564 -925,430 61,688,880.96 3.417 0.7164 09/30/2025
6 JPMorgan Securities LLC (Investment Management) 0 -907,679 0 0 0
7 Adar1 Capital Management LLC 1,350,826 -859,193 149,455,388.64 13.9601 1.7356 09/30/2025
8 Franklin Advisers, Inc. 516,090 -854,960 57,100,197.6 0.0252 0.6631 09/30/2025
9 Citadel Advisors LLC 516,679 -812,931 57,165,364.56 0.062 0.6639 09/30/2025
10 Kennedy Capital Management LLC 0 -225,191 0 0 0

Data provided by FactSet Research Systems Inc.